Merozyne – muscular dystrophy

Merozyne Therapeutics has been established to develop a treatment for MDC1A, a severe form of muscular dystrophy.

Merozyne – muscular dystrophy

merozyne

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Benitec – gene silencing by ddRNAi

DNA-directed RNA Interference (ddRNAi) is Benitec’s RNAi platform for gene silencing, with several advantages over other methods of gene silencing such as siRNA, anti-sense and zinc finger nucleases.

Benitec – gene silencing by ddRNAi

Benitec

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